Challenges are an inevitability when building a drug portfolio in the rare disease space, and patient finding is no doubt chief among them. Clinical trial recruitment is highly capital intensive,...

Though it’s not often discussed, often the most difficult aspect of bringing a drug to market is finding the right patient population. This is especially true with rare diseases, where patients...

Our own Julie Gubitosa and Graham Jones accompanied by Keith R. McCrae, MD of the Cleveland Clinic and Jennifer Beachell, Tricia Gooljarsingh PhD and Mary Lee Tjoa of Momenta Pharmaceutical,...